Judy George

The New England Journal of Medicine ©2026. A previously healthy 52-year-old woman entered the emergency department with a 4-month history of headaches and visual hallucinations.

Agency says deramiocel did not meet phase III trial endpoints, contrary to reported data

FDA scientists said that investigational deramiocel, a stem cell treatment for Duchenne muscular dystrophy, did not meet its primary endpoint in a

HHS delayed this week's Interagency Autism Coordinating Committee opens in a new tab or window meeting after advocates voiced concerns that the

— Long-term study looks at what happened when sugar was scarce Key Takeaways

— Novel analgesic associated with significantly lower opioid use Key Takeaways LTG-001, an investigational drug, reduced acute pain scores after abdominoplasty in a phase IIb trial.

Agency staff and drug developer disagree on endpoints

An FDA panel said that trial data did not provide substantial evidence showing that investigational deramiocel was effective in treating cardiomyopathy among patients with Duchenne muscular dystrophy.

Key Takeaways A study of nearly 2,800 U.S. boys found no evidence linking neonatal circumcision with autism.

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