By: Philipp Heher, Jakob Pfeiffer-Vogl, Massimo Ganassi, Raul-Cristian Fulea, Liam McGuire, Elise N Engquist, Johanna Prueller, Johannes Grillari, Giorgio Tasca, Christopher RS Banerji, Peter S Zammit, Jakob Pfeiff
Abstract Facioscapulohumeral muscular dystrophy (FSHD) is driven by DUX4-induced toxicity, yet the pathomechanisms remain unclear.





